Rare Disease Consulting

Greater understanding, treatment development and regulatory measures are introduced to encourage innovation in diseases with low prevalence and high unmet need. All of these aspects make it a very exciting time to work on rare disease.
Still, they represent a myriad of specifics that can be particularly challenging, including…
- The knowledge gaps/disease natural history is often poorly understood
- Not adapted standard trial designs
- Sometimes combined with no standardized definition
- The limited standard good practice guidelines
- The lengthy and complicated diagnosis pathway
- Specific regulatory pathways
- The overall lack of awareness
Get the right expertise, at the right time, for a winning market strategy.
R&D
We provide disease-specific data and insights to help you prioritize assets and pipeline.
Business development and licensing, Epidemiology, Forecasting, Health economics and outcomes research, KOL identification & influence mapping, Patient Preferences, Patient reported outcomes,Patient, physician, payer insights, Portfolio assessments & planning
Syndicated Data: Epi Database®, Forecast Architect®, CancerMpact®
Clinical Trials
We provide connected clinical and real-world solutions to optimize clinical trials and prepare you for submission.
Phase II-IV trials, Market access & value definition, Medical writing, Non interventional studies, Patient reported outcomes, Registries, Scientific Publications
Submission & Approval
We generate evidence of your product's safety and effectiveness so you can file with the confidence of a well-defined value proposition for all stakeholders.
Health economics and outcomes research, Market access, Pricing & Value definition, Risk-Benefit optimisation, Scientific Publications
Launch
We offer consultative approaches to ensure the success of your launch using connected commercial and real-world solutions.
Brand Strategy, Health economics and outcomes research, KOL identification & influence mapping, Market Understanding, Non interventional Studies, Patient, Physician insights, Patient reported outcomes, Patient Preferences, Risk Management Plan, Medical writing
Subscription Data: Epi Database®, Forecast Architect®, CancerMpact®
Post Marketing
We leverage real-world evidence to expand access through new indications with demonstrated product safety and value.
Brand Optimization, Health economics and outcomes research, Medical writing, Non interventional studies, Patient reported outcomes, Patient Preferences, Registries, Safety and Risk Management
Subscription Data: Epi Database®, Forecast Architect®, CancerMpact®
Also within Health
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Real-World Evidence
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Clinical Research & Medical Affairs
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Commercial Planning
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Specialist Consulting
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Data and Analytics